Refinement of antisense oligonucleotide mediated exon skipping as therapy for Duchenne muscular dystrophy
Heemskerk, J.A.
Citation
Heemskerk, J. A. (2011, October 26). Refinement of antisense
oligonucleotide mediated exon skipping as therapy for Duchenne muscular dystrophy. Retrieved from https://hdl.handle.net/1887/17986
Version: Corrected Publisher’s Version
License: Licence agreement concerning inclusion of doctoral thesis in the Institutional Repository of the University of Leiden
Downloaded from: https://hdl.handle.net/1887/17986
Note: To cite this publication please use the final published version (if applicable).
Chapter 3 Development of antisense-mediated exon skipping as a treatment for Duchenne muscular dystrophy
Heemskerk H
1, de Winter CL
1, van Ommen GJB
1, van Deutekom JCT
2and Aartsma-Rus A
11
Human Genetics, Leiden University Medical Center, the Netherlands
2
Prosensa Therapeutics, the Netherlands
Annals of the New York Academy of Sciences (2009) 1175, 71-9
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Development of exon skipping for DMD
